Cure STXBP1
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The Capsida clinical trial for its CAP 002 gene therapy for STXBP1 has been posted! - clinicaltrials.gov/study/NCT069...
trials.gov
May 21, 2025 at 6:32 PM
The Capsida clinical trial for its CAP 002 gene therapy for STXBP1 has been posted! - clinicaltrials.gov/study/NCT069...
Capsida Biotherapeutics has announced that it received approval from the FDA for its Investigational New Drug (IND) Application for its gene therapy CAP-002, developed for STXBP1-RD!
capsida.com/capsida-rece...
capsida.com/capsida-rece...
Capsida Receives FDA IND Clearance for Its First-in-Class, IV-administered Gene Therapy for STXBP1 Developmental and Epileptic Encephalopathy - Capsida Biotherapeutics
CAP-002 is the first engineered IV-delivered gene therapy that crosses the blood-brain-barrier and detargets the liver and dorsal root ganglia to enter the clinic THOUSAND OAKS, Calif., May 12, 2025 —...
capsida.com
May 14, 2025 at 4:18 PM
Capsida Biotherapeutics has announced that it received approval from the FDA for its Investigational New Drug (IND) Application for its gene therapy CAP-002, developed for STXBP1-RD!
capsida.com/capsida-rece...
capsida.com/capsida-rece...
The Q1 2025 census numbers are published! 1310 STX'ers! We found 83 patients this quarter! www.stxbp1disorders.org/news/stxbp1-...
STXBP1 Census - Q1 2025 — STXBP1 Foundation
1,310 Total Census · +83 Patients in Q1 2025
www.stxbp1disorders.org
April 5, 2025 at 6:38 PM
The Q1 2025 census numbers are published! 1310 STX'ers! We found 83 patients this quarter! www.stxbp1disorders.org/news/stxbp1-...