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DMD WarrioR
@dmdwarrior.com
43 followers 10 following 120 posts
Stay informed on #DMD cures, clinical trials, and #Duchenne muscular dystrophy research. Visit DMDWarrior.com for updates and support.
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Ractigen Therapeutics Doses First Patient in IIT Study of RAG-18, a Potential Game-Changing #saRNA Therapeutic for #Duchenne Muscular Dystrophy

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Ractigen Therapeutics Doses First Patient in IIT Study of RAG-18, a Potential Game-Changing #saRNA Therapeutic for #Duchenne Muscular Dystrophy Ractigen Therapeutics, a pioneering developer of small activating RNA (saRNA) therapeutics, today announced the successful dosing of the first patient in its investigator-initiated trial (IIT) of RAG-18 at Peking Union Medical College Hospital (PUMCH), Chinese Academy of Medical Sciences in Beijing. #DMD 👉 Read More: DMDWarrioR.com
December 12, 2025 at 3:07 PM
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Atossa Therapeutics Receives FDA Rare Pediatric Disease Designation for (Z)-Endoxifen for Duchenne Muscular Dystrophy

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Atossa Therapeutics Receives FDA Rare Pediatric Disease Designation for (Z)-Endoxifen for Duchenne Muscular Dystrophy Atossa Therapeutics announced that the U.S. Food and Drug Administration (“FDA”) has granted Rare Pediatric Disease (“RPD”) designation to (Z)-Endoxifen for the treatment of Duchenne Muscular Dystrophy (“DMD”). 👉 Read More: DMDWarrioR.com
December 11, 2025 at 2:06 PM
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Satellos reported that the FDA and other global regulators have cleared its IND for SAT-3247, enabling a three-month Phase 2, placebo-controlled trial in 51 ambulatory children with Duchenne muscular dystrophy. #satellos #dmd #duchenne

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Satellos Receives FDA and International Clearance to Commence Pediatric Phase 2 Testing of SAT-3247 for Duchenne Muscular Dystrophy Satellos reported that the FDA and other global regulators have cleared its IND for SAT-3247, enabling a three-month Phase 2, placebo-controlled trial in 51 ambulatory children with Duchenne muscular dystrophy. #satellos #dmd #duchenne 👉 Read More: DMDWarrioR.com
December 9, 2025 at 2:48 PM
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Researchers Buel D. Rodgers and Christopher W. Ward published a groundbreaking study in Gene Therapy that unveiled a codon-optimized human Smad7 gene therapy aimed at treating Duchenne muscular dystrophy (DMD).

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Researchers Develop Optimized Smad7 Gene Therapy to Target Duchenne Muscular Dystrophy Researchers Buel D. Rodgers and Christopher W. Ward published a groundbreaking study in Gene Therapy that unveiled a codon-optimized human Smad7 gene therapy aimed at treating Duchenne muscular dystrophy (DMD). 👉 Read More: DMDWarrioR.com
November 26, 2025 at 7:48 AM
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ELEVIDYS Gene Therapy for Non-Ambulant Children with DMD: FDA OKs ENDEAVOR Cohort 8 Immunosuppression Study

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ELEVIDYS Gene Therapy for Non-Ambulant Children with DMD: FDA OKs ENDEAVOR Cohort 8 Immunosuppression Study
November 25, 2025 at 3:19 PM
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Potential of SAT-3247 to Restore Muscle Regeneration in Duchenne Published in Nature

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Potential of SAT-3247 to Restore Muscle Regeneration in Duchenne Published in Nature Satellos Therapeutics announced that researchers at the Ottawa Hospital Research Institute have published new findings in Nature Communications validating the company’s innovative approach to treating the root cause of Duchenne muscular dystrophy and related diseases. 👉 Read More: DMDWarrioR.com
November 18, 2025 at 4:57 PM
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DMD ANKA mRNA therapy, currently under development for Duchenne muscular dystrophy in Turkiye, was announced by Associate Professor Dr. Ali Taghizadeh.

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Ali Taghizadeh Announces DMD ANKA mRNA Therapy, Currently in Clinical Trial in Turkiye DMD ANKA mRNA therapy, currently under development for Duchenne muscular dystrophy in Turkiye, was announced by Associate Professor Dr. Ali Taghizadeh.
November 17, 2025 at 2:11 PM
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REGENXBIO Announces Completion of RGX-202 Pivotal Enrollment and Initiates Commercial Production in Duchenne Gene Therapy Program

#dmd #duchenne #regenxbio #genetherapy #clinicaltrials #rgx202

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REGENXBIO Announces Completion of RGX-202 Pivotal Enrollment and Initiates Commercial Production in Duchenne Gene Therapy Program REGENXBIO announced it has completed enrollment of 30 participants in the pivotal portion of its AFFINITY DUCHENNE trial for RGX-202, an investigational gene therapy for Duchenne muscular dystrophy.
October 30, 2025 at 1:06 PM
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Hansa’ Imlifidase Reduce Anti-AAV Antibodies and Allow Administration of Gene Therapy

#dmd #duchenne #imlifidase #genetherapy #clinicaltrials

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Hansa’ Imlifidase Reduce Anti-AAV Antibodies and Allow Administration of Gene Therapy Two gene therapy trials, one sponsored by Sarepta and the other sponsored by Genethon, support the ability of imlifidase to substantially reduce anti-AAV antibodies to allow administration of gene therapy.
October 30, 2025 at 9:13 AM
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Why Elevidys Was Not Approved by the European Medicines Agency (EMA)?

You can access the comprehensive report on the reasons for the Elevidys refusal published by EMA from our web page link.

#dmd #duchenne #elevidys #eu

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If you're searching for answers to 'why Elevidys was not approved by the European Medicines Agency (EMA)', you're not alone. In this article, we explore the key reasons behind the EMA’s decision and what it means for patients, families, and the future of gene therapy in the EU.
October 22, 2025 at 10:13 AM
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Brogidirsen (NS-089/NCNP-02) has The Potential to Slow Disease Progression in DMD Patients Amenable to Exon 44 Skipping

#dmd #duchenne #exon44 #brogidirsen

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Brogidirsen (NS-089/NCNP-02) has The Potential to Slow Disease Progression in DMD Patients Amenable to Exon 44 Skipping Nippon Shinyaku announced efficacy and safety data from a 3.5-year application based on an open-label extension study that also included the initiation of a clinical trial for brogidirsen (NS-089/NCNP-02). #dmd #duchenne #exon44 #brogidirsen 👉 Read More: DMDWarrioR.com
October 14, 2025 at 7:34 AM
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Avidity Biosciences Announces Positive Pre-BLA Meeting with U.S. FDA for del-zota in DMD44 with a Submission Planned for Q1 2026

#dmd #duchenne #delzota #exon44 #exon44skipping #clinicaltrials #aviditybiosciences

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Avidity Biosciences Announces Positive Pre-BLA Meeting with U.S. FDA for del-zota in DMD44 with a Submission Planned for Q1 2026
October 13, 2025 at 1:28 PM
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Does Pulsed Electromagnetic Field (PEMF) Therapy Treat Duchenne Muscular Dystrophy and Initiate Dystrophin Production?

#pemf #dmd #duchenne

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Does Pulsed Electromagnetic Field (PEMF) Therapy Treat Duchenne Muscular Dystrophy and Initiate Dystrophin Production? In countries like Uzbekistan, information is being shared about the potential treatment of Duchenne Muscular Dystrophy with PEMF therapy. Pulsed Electromagnetic Field (PEMF) therapy is not a cure for Duchenne Muscular Dystrophy. Be careful not to let scammers take your money.
October 13, 2025 at 11:34 AM
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Tevard Biosciences Presents Data Demonstrating Production of Full-Length Protein with tRNA-Based Therapy for Duchenne Muscular Dystrophy

#dmd #duchenne
Tevard Biosciences Presents Data Demonstrating Production of Full-Length Protein with tRNA-Based Therapy for Duchenne Muscular Dystrophy Tevard Biosciences announced the presentation of new preclinical data showing potent restoration of full-length functional proteins in models of Duchenne muscular dystrophy (DMD) and dilated cardiomyopathy (DCM-TTNtv).
September 30, 2025 at 12:12 PM
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Cures of #Duchenne (Detailed List of All Clinical Trials for #DMD)

List of all researches such as #gene therapy, exon skipping, reducing inflammation and improving #muscle growth & protection cures for duchenne #muscular dystrophy.

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Cures of Duchenne (Detailed List of All Clinical Trials) List of all researches such as gene therapy, exon skipping, reducing inflammation and improving muscle growth & protection cures for duchenne muscular dystrophy.
September 28, 2025 at 11:14 AM
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Del-zota (Exon 44 Skipping Therapy) Demonstrated Reversal of Disease Progression Across Key Functional Endpoints in Phase 1/2 Trial

#dmd #duchenne #delzota #exon44 #exon44skipping #clinicaltrials #aviditybiosciences

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Del-zota (Exon 44 Skipping Therapy) Demonstrated Reversal of Disease Progression Across Key Functional Endpoints in Phase 1/2 Trial With del-zota, normal dystrophin increased by 25% and creatine kinase decreased by 80%. Among exon 44 skipping therapies, the highest values ​​currently received have caused excitement. Unprecedented rapid reduction in creatine kinase (CK) to near normal levels maintained over 16 months of follow-up and 25% increase of normal in dystrophin production, reflecting sustained muscle fiber protection.
September 10, 2025 at 12:27 PM
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Belief BioMed Announced Successful Completion of First Dose of BBM-D101 Gene Therapy

#dmd #duchenne #BBMD101 #BeliefBioMed #clinicaltrials

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Belief BioMed Announced Successful Completion of First Dose of BBM-D101 Gene Therapy Belief BioMed, an innovative biotechnology company focused on developing cutting-edge gene therapies, today announced that the registration clinical trial (CTR20252461) of its independently developed and produced BBM-D101 injection for Duchenne Muscular Dystrophy (DMD) has successfully completed the first patient dosing in Beijing, China.
September 9, 2025 at 3:24 PM
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Solid Biosciences Initiates Phase 3 Clinical Trial of SGT-003 Gene Therapy (IMPACT DUCHENNE) in Ambulant Males

#dmd #duchenne #sgt003 #genetherapy #clinicaltrials

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Solid Biosciences Initiates Phase 3 Clinical Trial of SGT-003 Gene Therapy (IMPACT DUCHENNE) in Ambulant Males The phase 3 study (NCT07160634) of the SGT-003 gene therapy developed by Solid Biosciences is expected to begin in October 2025 and be completed in January 2029. The SGT-003 Phase 3 study will include 80 ambulant males, moreover the study locations have not yet been shared.
September 9, 2025 at 11:17 AM
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Keros Therapeutics Presents Additional Clinical Data from its KER-065 Program at the American Society of Bone and Mineral Research 2025 Annual Meeting

#dmd #duchenne #ker065

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Keros Therapeutics Presents Additional Clinical Data from its KER-065 Program at the American Society of Bone and Mineral Research 2025 Annual Meeting Phase 1 Trial in Healthy Participants of KER-065, a Modified Activin Receptor Ligand Trap, Supports Development in Duchenne Muscular Dystrophy and Bone Disorders.
September 8, 2025 at 4:39 PM
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GNR-097: Duchenne Gene Therapy Phase 1/2 Study Started by Generium

Generium is a Russian innovative biotechnology company has received approval to conduct a clinical trial of GNR-097 gene therapy drug for the treatment of progressive Duchenne muscular dystrophy (DMD).

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GNR-097: Duchenne Gene Therapy Phase 1/2 Study Started by Generium Generium is a Russian innovative biotechnology company has received approval to conduct a clinical trial of GNR-097 gene therapy drug for the treatment of progressive Duchenne muscular dystrophy (DMD). The multicenter, single-blind, randomized placebo-controlled trial involves a single intravenous administration of the gene therapy drug to pediatric patients with progressive Duchenne muscular dystrophy. This Phase 1/2 study aims to evaluate the tolerability, safety, and efficacy of the drug GNR-097. #dmd #duchenne #gnr097 #genetherapy #clinicaltrials 👉 Read More: DMDWarrioR.com
September 7, 2025 at 10:47 AM
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🎈 SEPTEMBER 7, 2025 🎈

Support World Duchenne Awareness Day 2025 with DMDWarrior

Theme of 2025: Make Cures Affordable for Duchenne

#WorldDuchenneAwarenessDay #dmdwarrior #SupportDuchenne #DMD #WDAD #UntilEveryoneHasACure #TogetherWeThrive #Becker #MuscularDystrophy #ExonSkipping
🎈 SEPTEMBER 7, 2025 🎈 Support World Duchenne Awareness Day 2025 with DMDWarrior Theme of 2025: Make Cures Affordable for Duchenne We’re inviting YOU to stand with the #DuchenneCommunity and #DMDWarrior. Every post raises awareness. Every tag sparks a conversation. Every share brings us closer to a cure. 🚀 Be sure to tag @dmdwarrior and use these hashtags to amplify your impact: #WorldDuchenneAwarenessDay #dmdwarrior #SupportDuchenne #DMD #WDAD #UntilEveryoneHasACure #TogetherWeThrive #Becker #MuscularDystrophy #ExonSkipping 💪 Together We Are Stronger 🎈 SEPTEMBER 7, 2025 🎈 Support World Duchenne Awareness Day 2025 with DMDWarrior Theme of 2025: Make Cures Affordable for Duchenne We’re inviting YOU to stand with the #DuchenneCommunity and #DMDWarrior. Every post raises awareness. Every tag sparks a conversation. Every share brings us closer to a cure. 🚀 Be sure to tag @dmdwarrior and use these hashtags to amplify your impact: #WorldDuchenneAwarenessDay #dmdwarrior #SupportDuchenne #DMD #WDAD #UntilEveryoneHasACure #TogetherWeThrive #Becker #MuscularDystrophy #ExonSkipping 💪 Together We Are Stronger 🎈 SEPTEMBER 7, 2025 🎈 Support World Duchenne Awareness Day 2025 with DMDWarrior Theme of 2025: Make Cures Affordable for Duchenne We’re inviting YOU to stand with the #DuchenneCommunity and #DMDWarrior. Every post raises awareness. Every tag sparks a conversation. Every share brings us closer to a cure. 🚀 Be sure to tag @dmdwarrior and use these hashtags to amplify your impact: #WorldDuchenneAwarenessDay #dmdwarrior #SupportDuchenne #DMD #WDAD #UntilEveryoneHasACure #TogetherWeThrive #Becker #MuscularDystrophy #ExonSkipping 💪 Together We Are Stronger
September 6, 2025 at 10:12 AM
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How Does My Child Participate in Clinical Trials for Duchenne?

Learn how your child can join Duchenne muscular dystrophy (DMD) clinical trials and discover trusted resources to find active studies near you.

Learn More 👇

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How Does My Child Participate in Clinical Trials for Duchenne? Learn how your child can join Duchenne muscular dystrophy (DMD) clinical trials and discover trusted resources to find active studies near you. If your child has been diagnosed with Duchenne muscular dystrophy (DMD), you may be exploring every possible option for treatment and care—including clinical trials. But how does your child participate in a Duchenne clinical trial? And where can you find trials that are actively recruiting?
September 6, 2025 at 10:10 AM
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🎈 SEPTEMBER 7, 2025 🎈

Support World Duchenne Awareness Day 2025 with DMDWarrior

Theme of 2025: Make Cures Affordable for Duchenne

#WorldDuchenneAwarenessDay #dmdwarrior #SupportDuchenne #DMD #WDAD
#UntilEveryoneHasACure #TogetherWeThrive #Becker #MuscularDystrophy #ExonSkipping
Support World Duchenne Awareness Day 2025 with DMDWarrior World Duchenne Awareness Day will be observed globally on September 7, 2025, with the theme “Make Cures Affordable for Duchenne.” This important day raises awareness about Duchenne Muscular Dystrophy (DMD), a rare genetic condition that causes progressive muscle weakness and affects thousands of individuals and families worldwide. Each year, the campaign calls for more attention, research, and action toward better treatments and, ultimately, a cure. Theme of 2025: Make Cures Affordable for Duchenne This year’s theme reflects the urgent and universal wish of the Duchenne community: access to effective and affordable cures for Duchenne Muscular Dystrophy (DMD). Families, patients, and advocacy groups are united in calling for equitable access to treatments, accelerated research, and global collaboration.
August 30, 2025 at 1:32 PM
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ITF Therapeutics Announces Publication of Positive Long-Term Data Reinforcing Duvyzat (Givinostat) Efficacy and Safety as a Treatment for Duchenne Muscular Dystrophy

#givinostat #duvyzat

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ITF Therapeutics Announces Publication of Positive Long-Term Data Reinforcing Duvyzat (Givinostat) Efficacy and Safety as a Treatment for Duchenne Muscular Dystrophy Positive long-term safety and efficacy data for Duvyzat (Givinostat) as a treatment for Duchenne muscular dystrophy (DMD) were published today by ITF Therapeutics, an Italfarmaco affiliate. The data came from the company's open-label extensions of its Phase 2 and Phase 3 (EPIDYS) trials. 🎈 New data published in Annals of Clinical and Translational Neurology show that long-term treatment with givinostat can significantly delay loss of key mobility functions in patients with Duchenne muscular dystrophy. 🎈 Meaningful clinical benefit was observed across treatment groups, regardless of disease stage at initiation. 🎈 Givinostat remained well-tolerated during extended use, consistent with previous clinical trials. 🎈 Average follow-up in the extension study exceeded 36 treatment months, with some patients receiving treatment for over eight years since initiating givinostat treatment. #givinostat #duvyzat 👉 Read More: DMDWarrioR.com
August 25, 2025 at 2:42 PM
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Agamree to be sold in United Arab Emirates, Saudi Arabia, Kuwait, Oman and Bahrain starting in 2026

#agamree #vamorolone #uae #bahrain #oman #saudi_arabia #kuwait

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Agamree to be sold in United Arab Emirates, Saudi Arabia, Kuwait, Oman and Bahrain starting in 2026 Santhera Pharmaceuticals announces the signing of an exclusive agreement with Uniphar to manage the distribution of AGAMREE (vamorolone) in the United Arab Emirates, the Kingdom of Saudi Arabia, Kuwait, Oman and Bahrain, for the treatment of Duchenne muscular dystrophy (DMD) in patients four years of age and older.
August 19, 2025 at 7:39 AM