Loubet Michel
@loubetmichel.bsky.social
CNS Webinar: Duchenne Muscular Dystrophy: Connecting the Dots Between Pathophysiology and Treatment
www.childneurologysociety.org/event/cns-we...
www.childneurologysociety.org/event/cns-we...
CNS Webinar: Duchenne Muscular Dystrophy: Connecting the Dots Between Pathophysiology and Treatment - Child Neurology Society
Click for more information.
www.childneurologysociety.org
December 2, 2025 at 11:16 AM
CNS Webinar: Duchenne Muscular Dystrophy: Connecting the Dots Between Pathophysiology and Treatment
www.childneurologysociety.org/event/cns-we...
www.childneurologysociety.org/event/cns-we...
Reposted by Loubet Michel
Serge Braun, directeur de la stratégie neuromusculaire de Généthon, raconte comment la recherche a ouvert une nouvelle voie thérapeutique pour la myopathie de Duchenne.
👉 https://www.telethon2025.fr
👉 https://www.telethon2025.fr
Myopathie de Duchenne : l'épopée de la thérapie génique (avec Serge Braun)
Des premières découvertes aux victoires d’aujourd’hui, Serge Braun raconte comment la recherche a ouvert une nouvelle voie pour les enfants atteints de myopa...
youtu.be
November 27, 2025 at 9:32 AM
Serge Braun, directeur de la stratégie neuromusculaire de Généthon, raconte comment la recherche a ouvert une nouvelle voie thérapeutique pour la myopathie de Duchenne.
👉 https://www.telethon2025.fr
👉 https://www.telethon2025.fr
"Immune cells use a surprising trick to heal muscle faster"
www.sciencedaily.com/releases/202...
www.sciencedaily.com/releases/202...
Immune cells use a surprising trick to heal muscle faster
A research team has found that specific immune cells can connect with muscle fibers in a lightning-fast, neuron-like way to promote healing. These cells deliver quick pulses of calcium, triggering rep...
www.sciencedaily.com
November 25, 2025 at 12:30 PM
"Immune cells use a surprising trick to heal muscle faster"
www.sciencedaily.com/releases/202...
www.sciencedaily.com/releases/202...
Reposted by Loubet Michel
Proud to partner with @eurordis for #ECRD2026, Europe’s largest patient-led rare disease event. Join us in Prague & online, 3–4 June 2026. Poster abstracts now open! 👉 www.rare-diseases.eu/posters
November 21, 2025 at 10:48 AM
Proud to partner with @eurordis for #ECRD2026, Europe’s largest patient-led rare disease event. Join us in Prague & online, 3–4 June 2026. Poster abstracts now open! 👉 www.rare-diseases.eu/posters
Reposted by Loubet Michel
📚 New from REMEDi4ALL: A major review in the British Journal of Pharmacology identifies 33 policy barriers holding back drug repurposing in Europe.
A key step toward better policies & improved patient access to repurposed treatments.
👉 https://bpspubs.onlinelibrary.wiley.com/doi/10.1111/bph.70243
A key step toward better policies & improved patient access to repurposed treatments.
👉 https://bpspubs.onlinelibrary.wiley.com/doi/10.1111/bph.70243
November 22, 2025 at 8:00 AM
📚 New from REMEDi4ALL: A major review in the British Journal of Pharmacology identifies 33 policy barriers holding back drug repurposing in Europe.
A key step toward better policies & improved patient access to repurposed treatments.
👉 https://bpspubs.onlinelibrary.wiley.com/doi/10.1111/bph.70243
A key step toward better policies & improved patient access to repurposed treatments.
👉 https://bpspubs.onlinelibrary.wiley.com/doi/10.1111/bph.70243
Reposted by Loubet Michel
MHRA reforms mark a vital step toward faster, safer innovation for the 500M people worldwide living with rare diseases.
A more adaptive, evidence-based framework will help researchers and clinicians deliver life-changing therapies faster.
Read more: tinyurl.com/msurx5ju
A more adaptive, evidence-based framework will help researchers and clinicians deliver life-changing therapies faster.
Read more: tinyurl.com/msurx5ju
New drugs to be approved faster so patients don’t wait years
The medicines watchdog is changing how it oversees research of 7,000 rare diseases, which collectively affect about one in 17 Britons
tinyurl.com
November 3, 2025 at 4:22 PM
MHRA reforms mark a vital step toward faster, safer innovation for the 500M people worldwide living with rare diseases.
A more adaptive, evidence-based framework will help researchers and clinicians deliver life-changing therapies faster.
Read more: tinyurl.com/msurx5ju
A more adaptive, evidence-based framework will help researchers and clinicians deliver life-changing therapies faster.
Read more: tinyurl.com/msurx5ju