#AIPL1
$MGTX +5% [Eli Lilly partners with MeiraGTx in a $475M deal for a breakthrough gene therapy, AAV-AIPL1, designed to restore vision in children born legally blind.] notreload.xyz/eli-lilly-me...
Eli Lilly, MeiraGTx Ink $475M Vision Gene Therapy Deal
Eli Lilly partners with MeiraGTx in a $475M deal for a breakthrough gene therapy, AAV-AIPL1, designed to restore vision in children born legally blind.
notreload.xyz
November 10, 2025 at 3:57 PM
genomirx.com/shop/novus-b...

NOVUS BIOLOGICALS AIPL1 Polyclonal antibody detects AIPL1 in Human, Mouse, Rat samples. It is validated for Western Blot, ELISA, Immunocytochemistry (Paraffin)
Novus Scientific Inc @novusbio.bsky.social #AILP1 #Elisa #Polyclonal #antibody #detects
November 2, 2025 at 7:31 PM
Un ensayo clínico en The Lancet logró restaurar visión parcial en niños con ceguera genética mediante terapia génica con el gen AIPL1. El avance abre nuevas posibilidades para tratar otras enfermedades oculares y condiciones hereditarias complejas.
October 3, 2025 at 9:30 AM
Jace born completely blind regained partial vision after receiving experimental gene therapy in London Great Ormond Street and Moorfields Eye Hospital injected a working copy of the faulty AIPL1 gene directly into his retina www.ctinsider.com/living/artic...
July 3, 2025 at 1:04 AM
Six-year-old Jace Broadbin, born blind due to Leber congenital amaurosis (LCA), a genetic condition caused by mutations in the AIPL1 gene, has regained partial vision through a pioneering gene therapy.

#GeneTherapy #MedicalBreakthrough #ChildhoodBlindness #LCA #VisionRestoration
May 1, 2025 at 8:50 AM
Six-year-old Jace Broadbin, born blind due to Leber congenital amaurosis (LCA), a genetic condition caused by mutations in the AIPL1 gene, has regained partial vision through a pioneering gene therapy.

#GeneTherapy #MedicalBreakthrough #ChildhoodBlindness #LCA #VisionRestoration
April 30, 2025 at 6:03 PM
Ophthopedia Update: Week in Review: Genetic Therapy for Severe Retinal Dystrophy, Effect of Cocoa Extract on AMD, OCT for Diagnosing Major Depressive Disorder: A genetic therapy to help patients with AIPL1-related retinal dystrophy gets its first in-human tryout, taking cocoa… #Ophthalmology #News
Week in Review: Genetic Therapy for Severe Retinal Dystrophy, Effect of Cocoa Extract on AMD, OCT for Diagnosing Major Depressive Disorder
A genetic therapy to help patients with AIPL1-related retinal dystrophy gets its first in-human tryout, taking cocoa extract does not appear to reduce the rate of AMD occurrence, and OCT may have a use in diagnosing major depressive disorder.
dlvr.it
April 11, 2025 at 3:07 PM
MAGIK: Human cone #photoreceptor transplantation in an AIPL1 model of end-stage Leber congenital amaurosis drives retinal remodeling & function, with light-evoked head-tracking behavior at physiologically relevant light levels
ow.ly/cVnA50Vq3nq

@isscr.org
March 27, 2025 at 7:59 PM
Healthy copies of the AIPL1 gene were injected into their retinas, enabling them to see shapes, recognize faces, and even read and write.

When will #ME be the next miracle discovery?

2
March 13, 2025 at 8:59 PM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 11:09 AM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 10:09 AM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 9:09 AM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 8:09 AM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 7:09 AM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 6:09 AM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 5:09 AM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 4:09 AM
英MeiraGTx社、AIPL1変異関連の網膜ジストロフィーの遺伝子治療で小児患者の視力が改善 - 日経バイオテク
news.google.com/rss/articles/CBMiZkFVX3lxTE1HSm5MRHhiazh0U09fcDgyei16UVlBSmNqc2xTN3FQM18tT1VvalVHeTIyMEVaenBMRDNjZlZ5eFRBTDhiM0s1bXpSMlE2T2I0ekM3alhVNjNaRzdBRU5RZHNHMVdsUQ?oc=5
March 12, 2025 at 3:09 AM
AIPL1関連重度網膜ジストロフィー、アデノ随伴ウイルスベクターで視力改善/Lancet|CareNet.com - CareNet.com
news.google.com/rss/articles/CBMiX0FVX3lxTFBZY05qUGNMWnU2SzRVbTU5Y3BPekZUSGNXek5ackJkWVhmZkxCcTQxOElxT2JlWmN4UHV6ZVY4b3NkTmFiUVJWb2lRdmtZMWs2Z2VUamw4NlZ6VkNYbkFn?oc=5
March 6, 2025 at 3:09 PM
AIPL1関連重度網膜ジストロフィー、アデノ随伴ウイルスベクターで視力改善/Lancet|CareNet.com - CareNet.com
news.google.com/rss/articles/CBMiX0FVX3lxTFBZY05qUGNMWnU2SzRVbTU5Y3BPekZUSGNXek5ackJkWVhmZkxCcTQxOElxT2JlWmN4UHV6ZVY4b3NkTmFiUVJWb2lRdmtZMWs2Z2VUamw4NlZ6VkNYbkFn?oc=5
March 6, 2025 at 2:09 PM
AIPL1関連重度網膜ジストロフィー、アデノ随伴ウイルスベクターで視力改善/Lancet|CareNet.com - CareNet.com
news.google.com/rss/articles/CBMiX0FVX3lxTFBZY05qUGNMWnU2SzRVbTU5Y3BPekZUSGNXek5ackJkWVhmZkxCcTQxOElxT2JlWmN4UHV6ZVY4b3NkTmFiUVJWb2lRdmtZMWs2Z2VUamw4NlZ6VkNYbkFn?oc=5
March 6, 2025 at 1:09 PM
AIPL1関連重度網膜ジストロフィー、アデノ随伴ウイルスベクターで視力改善/Lancet|CareNet.com - CareNet.com
news.google.com/rss/articles/CBMiX0FVX3lxTFBZY05qUGNMWnU2SzRVbTU5Y3BPekZUSGNXek5ackJkWVhmZkxCcTQxOElxT2JlWmN4UHV6ZVY4b3NkTmFiUVJWb2lRdmtZMWs2Z2VUamw4NlZ6VkNYbkFn?oc=5
March 6, 2025 at 12:09 PM
AIPL1関連重度網膜ジストロフィー、アデノ随伴ウイルスベクターで視力改善/Lancet|CareNet.com - CareNet.com
news.google.com/rss/articles/CBMiX0FVX3lxTFBZY05qUGNMWnU2SzRVbTU5Y3BPekZUSGNXek5ackJkWVhmZkxCcTQxOElxT2JlWmN4UHV6ZVY4b3NkTmFiUVJWb2lRdmtZMWs2Z2VUamw4NlZ6VkNYbkFn?oc=5
March 6, 2025 at 11:09 AM
AIPL1関連重度網膜ジストロフィー、アデノ随伴ウイルスベクターで視力改善/Lancet|CareNet.com - CareNet.com
news.google.com/rss/articles/CBMiX0FVX3lxTFBZY05qUGNMWnU2SzRVbTU5Y3BPekZUSGNXek5ackJkWVhmZkxCcTQxOElxT2JlWmN4UHV6ZVY4b3NkTmFiUVJWb2lRdmtZMWs2Z2VUamw4NlZ6VkNYbkFn?oc=5
March 6, 2025 at 10:09 AM